Lucas, from Belgium, was 6 years old when he was diagnosed with brain stem cancer. He enrolled in the Biological Medicine Study for DIPG Eradication (BIOMEDE) The 13-year-old was treated with everolimus, which completely eliminated his tumor.

"I don't know of another case like it in the world," said the study's principal investigator, Dr. Jacques Grill. The road is still long, as effective treatment for the disease is still a long way off, says Grill.